Gene therapy saved Connie Burnett-West from a grim lung cancer diagnosis in 1999 – she had no other options. Today she remains cancer free.
Five years ago, another lung-cancer patient, also near the end of life, participated in a trial at the University of Miami using a gene therapy vaccine that boosts the impact of chemotherapy, without side effects, and she is still in remission.
PROGRESS
| 1990 | FDA approves first gene therapy study on a young patient treated for ADA-SCID. |
| 2010 | Three patients dying of leukemia, including a child, now in remission because of a clinical trial at the University of Pennsylvania, based on research funded by ACGT. |
| 2012 | First gene therapy drug, Glybera, approved by the European Medicines Agency, in review by FDA. |
| 2013 | Human Gene Therapy magazine names 4 ACGT scientists top pioneers in cell and gene therapies. |
| 2014 | Over 1,000 gene therapy trials completed or ongoing worldwide. |
